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- Huntington's_disease_clinical_research abstract "Huntington's disease is a genetic neurological disorder characterized after onset by uncoordinated, jerky body movements and a decline in some mental abilities for which there is no present cure or effective treatments.Research into the mechanism of Huntington's disease (HD) has focused on identifying the functioning of the huntingtin protein (Htt), how mutant huntingtin (mHtt) differs or interferes with it, and the brain pathology that the disease produces. Research is conducted using in vitro methods, animal models and human volunteers. Animal models are critical for understanding the fundamental mechanisms causing the disease and for supporting the early stages of drug development. The identification of the causative gene has enabled the development of many transgenic animal models including nematode worms, Drosophila fruit flies, mice, rats, sheep, pigs and monkeys that express mutant huntingtin and develop progressive neurodegeneration and HD-like symptoms.Three broad approaches are under study to attempt to slow the progression of Huntington's disease: reducing production of the mutant protein, improving cells' ability to survive its diverse harmful effects, and replacing lost neurons.".
- Huntington's_disease_clinical_research thumbnail PDB_3io4_EBI.png?width=300.
- Huntington's_disease_clinical_research wikiPageExternalLink chdifoundation.org.
- Huntington's_disease_clinical_research wikiPageExternalLink euro-hd.net.
- Huntington's_disease_clinical_research wikiPageExternalLink hdbuzz.net.
- Huntington's_disease_clinical_research wikiPageExternalLink hddrugworks.org.
- Huntington's_disease_clinical_research wikiPageExternalLink hdyo.org.
- Huntington's_disease_clinical_research wikiPageExternalLink hopes.stanford.edu.
- Huntington's_disease_clinical_research wikiPageExternalLink www.hdfoundation.org.
- Huntington's_disease_clinical_research wikiPageExternalLink www.huntington-study-group.org.
- Huntington's_disease_clinical_research wikiPageID "21999053".
- Huntington's_disease_clinical_research wikiPageRevisionID "604436215".
- Huntington's_disease_clinical_research hasPhotoCollection Huntington's_disease_clinical_research.
- Huntington's_disease_clinical_research subject Category:Extrapyramidal_and_movement_disorders.
- Huntington's_disease_clinical_research subject Category:Genetic_disorders.
- Huntington's_disease_clinical_research subject Category:Huntington's_disease.
- Huntington's_disease_clinical_research subject Category:Systemic_atrophies_primarily_affecting_the_central_nervous_system.
- Huntington's_disease_clinical_research type Abstraction100002137.
- Huntington's_disease_clinical_research type Attribute100024264.
- Huntington's_disease_clinical_research type Condition113920835.
- Huntington's_disease_clinical_research type Disease114070360.
- Huntington's_disease_clinical_research type GeneticDisease114151139.
- Huntington's_disease_clinical_research type GeneticDisorders.
- Huntington's_disease_clinical_research type IllHealth114052046.
- Huntington's_disease_clinical_research type Illness114061805.
- Huntington's_disease_clinical_research type PathologicalState114051917.
- Huntington's_disease_clinical_research type PhysicalCondition114034177.
- Huntington's_disease_clinical_research type State100024720.
- Huntington's_disease_clinical_research comment "Huntington's disease is a genetic neurological disorder characterized after onset by uncoordinated, jerky body movements and a decline in some mental abilities for which there is no present cure or effective treatments.Research into the mechanism of Huntington's disease (HD) has focused on identifying the functioning of the huntingtin protein (Htt), how mutant huntingtin (mHtt) differs or interferes with it, and the brain pathology that the disease produces.".
- Huntington's_disease_clinical_research label "Huntington's disease clinical research".
- Huntington's_disease_clinical_research sameAs m.05p3psz.
- Huntington's_disease_clinical_research sameAs Q17155104.
- Huntington's_disease_clinical_research sameAs Q17155104.
- Huntington's_disease_clinical_research sameAs Huntington's_disease_clinical_research.
- Huntington's_disease_clinical_research wasDerivedFrom Huntington's_disease_clinical_research?oldid=604436215.
- Huntington's_disease_clinical_research depiction PDB_3io4_EBI.png.
- Huntington's_disease_clinical_research isPrimaryTopicOf Huntington's_disease_clinical_research.